Eculizumab vs placebo
Transfusion independence · patients with paroxysmal nocturnal hemoglobinuria
Eculizumab probably leads to higher transfusion independence compared with placebo (moderate certainty).
1 finding from 1 review
- Eculizumab for treating patients with paroxysmal nocturnal hemoglobinuria 2014 · Cochrane Headline outcomes onlyRR 46.02 [2.88, 735.53]1 study · 87 participantsModerate