Findings

What do systematic reviews say?

10 questions · 10 findings · 5 reviews · Neuromuscular

Sort:Best matchNewest Highest certainty Download CSV

No studies found 5 · 50%GRADE not reported 2 · 20%Very low 0 · 0%Low 1 · 10%Moderate 2 · 20%High 0 · 0%

Inotersen vs placebo

QoL · people with TTR‐FAP

1 finding from 1 review

Pharmacological treatment for familial amyloid polyneuropathy 2020 · Cochrane Headline outcomes only
no estimate extracted
1 study · 172 participants
Low

Lisinopril (0.7 mg/kg daily) vs losartan (0.7 mg/kg daily)

Improvements in quality of life measures · patients with established cardiomyopathy in DMD

The review found no eligible studies for this question.

1 finding from 1 review

Interventions for preventing and treating cardiac complications in Duchenne and Becker muscular dystrophy and X‐linked… 2018 · Cochrane Headline outcomes only
no estimate extracted
Studies not reported
No studies found

α‐tocopheryl quinone vs placebo

Short‐term (within 1 month) change in quality of life scores related to communication as measured by validated communication assessments · people with speech disorder resulting from hereditary ataxias

1 finding from 1 review

Treatment for speech disorder in Friedreich ataxia and other hereditary ataxia syndromes 2014 · Cochrane Headline outcomes only
no estimate extracted
0 studies · 0 participants
GRADE not reported

α‐tocopheryl quinone vs placebo

Longer‐term (minimum 1 month) change in generic quality of life scores · people with speech disorder resulting from hereditary ataxias

1 finding from 1 review

Treatment for speech disorder in Friedreich ataxia and other hereditary ataxia syndromes 2014 · Cochrane Headline outcomes only
no estimate extracted
1 study · 19 participants
Moderate

Intervention not reported

Health‐related quality of life · participants with relapsed or recurrent CTEV

The review found no eligible studies for this question.

1 finding from 1 review

Interventions for congenital talipes equinovarus (clubfoot) 2020 · Cochrane Headline outcomes only
no estimate extracted
Studies not reported
No studies found

Intervention not reported

Health‐related quality of life · participants with neglected CTEV

The review found no eligible studies for this question.

1 finding from 1 review

Interventions for congenital talipes equinovarus (clubfoot) 2020 · Cochrane Headline outcomes only
no estimate extracted
Studies not reported
No studies found

Intervention not reported

Health‐related quality of life · participants with CTEV (type of case (i.e. whether initial presentation or relapsed) not specified)

The review found no eligible studies for this question.

1 finding from 1 review

Interventions for congenital talipes equinovarus (clubfoot) 2020 · Cochrane Headline outcomes only
no estimate extracted
Studies not reported
No studies found

Intervention not reported

Health‐related quality of life · participants with CTEV at initial presentation

1 finding from 1 review

Interventions for congenital talipes equinovarus (clubfoot) 2020 · Cochrane Headline outcomes only
no estimate extracted
2 studies · 2 participants
GRADE not reported

Intervention not reported

Health‐related quality of life · participants with resistant CTEV

The review found no eligible studies for this question.

1 finding from 1 review

Interventions for congenital talipes equinovarus (clubfoot) 2020 · Cochrane Headline outcomes only
no estimate extracted
Studies not reported
No studies found

Intervention not reported

Health‐related quality of life Short Form 12 Health Survey (SF‐12) · people with ALS/MND

1 finding from 1 review

Gamma aminobutyric acid (GABA) modulators for amyotrophic lateral sclerosis/motor neuron disease 2017 · Cochrane Headline outcomes only
no estimate extracted
1 study · 128 participants
Moderate