Ataluren vs placebo
Sweat chloride level ‐ change from baseline Scale: mmol/L · adults and children with CF with at least one class I mutation (PTC)
1 finding from 1 review
- Ataluren and similar compounds (specific therapies for premature termination codon class I mutations) for cystic… 2023 · Cochrane Headline outcomes onlyno estimate extracted1 study · 194 participantsHigh