Ataluren vs placebo
FEV1 % predicted: relative change from baseline · adults and children with CF with at least one class I mutation (PTC)
1 finding from 1 review
- Ataluren and similar compounds (specific therapies for premature termination codon class I mutations) for cystic… 2023 · Cochrane Headline outcomes onlyno estimate extracted1 study · 203 participantsHigh