Ataluren vs placebo
Nutrition and growth Change in: a) weight (kg) b) BMI (kg/m2) c) height (m) · adults and children with CF with at least one class I mutation (PTC)
1 finding from 1 review
- Ataluren and similar compounds (specific therapies for premature termination codon class I mutations) for cystic… 2023 · Cochrane Headline outcomes onlyno estimate extracted2 studies · 506 participantsHigh