Intrathecal injected nusinersen vs sham
Change in disability score (3 point‐change) · children with SMA type II
Intrathecal injected nusinersen showed no clear difference in change in disability score (3 point‐change) compared with sham procedure (moderate certainty).
1 finding from 1 review
- RR 1.8 [0.99, 3.1]1 study · 126 participantsModerate